Behavioral and histological hallmarks of a mucopolysaccharidosis type IIIA mouse model
Vera Niederkofler1, Ewald Auer1, David Amschl1, Joerg Neddens1, Elisabet Ohlin Sjöström2, Susanne Gustavsson2, Birgit Hutter-Paier1
1QPS Austria GmbH, Parkring 12, 8074 Grambach, AUSTRIA, 2Research & Translational Science, Swedish Orphan Biovitrum AB, Stockholm, SWEDEN