CAR-T is an immunotherapy that is currently used to treat blood…
Category: Gene Therapy
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While research on potential therapeutic applications of mRNA has been underway…
Biotech start-up Ring Therapeutics, founded by Flagship Pioneering in 2017, hopes…
An estimated 650 million adults live with obesity today, which puts…
Transthyretin amyloidosis (ATTR amyloidosis) is a rare but fatal disease marked…
Depending on your perspective, giraffes are either the world’s most graceful…
As a hereditary trait, eye color tends to be an introductory…
Osteoarthritis is a debilitating and painful wearing down of joint cartilage…
RNA viruses are known to cause a large number of diseases…
Contract research organizations (CROs) have been an integral part of drug…
Although you might think of the ability to hop as one…
A common refrain in science fiction movies is the cautionary statement,…
Cell and gene therapies (CGTs) are quickly making their way from…
Whether you adore cats or you’re allergic to them, you might…
Danon Disease is a rare, life-threatening condition in which the body’s…
Inherited retinal diseases (IRDs) can cause vision loss that ranges from…
Squid have long been a key organism for deepening the understanding…
There is new hope for future innovation in the fast-moving field…
On January 28, 2020, the United States Food and Drug Administration…
The heterogeneous presentation of clinical cases and the complex requirements by…
Introduction Researchers are developing novel, safer treatments for cancer, but bringing new oncology therapies to market is challenging. This white paper will examine the…
Introduction As global obesity rates continue to rise, the search for effective treatments is more critical than ever. Obesity is associated with an increased…
Introduction Changes in how clinical trials are managed in the European Union (EU), mandated by the European Union Clinical Trial Regulation 536/2014 (EU CTR),…
NEWARK, Delaware, November 13, 2024/BUSINESS WIRE/ — QPS Holdings, LLC announced today that their Springfield campus, QPS Missouri, has launched a new Cell Therapy…
NEWARK, Delaware, June 26, 2024/BUSINESS WIRE/ — QPS Holdings, LLC (QPS), a leading global contract research organization (CRO), is pleased to announce new laboratory…
NEWARK, Delaware, June 10, 2024/BUSINESS WIRE/ — QPS Holdings, LLC (QPS), a leading global contract research organization (CRO), is pleased to announce new clinical…
CRISPR and the Continuing Quest for CAR-T Safety and Durability
October 27, 2021
CAR-T is an immunotherapy that is currently used to treat blood cancers and is in clinical trials to treat other cancers as well. This treatment
mRNA: Great Expectations vs. Limited Applications
October 18, 2021
While research on potential therapeutic applications of mRNA has been underway for more than a decade, the success of the Pfizer and Moderna COVID-19 vaccines
Move Over AAV – Anelloviruses May Be Key to NextGen Gene Therapy
September 27, 2021
Biotech start-up Ring Therapeutics, founded by Flagship Pioneering in 2017, hopes to transform gene therapy by using a new class of vector — anelloviruses –
A Genetic Game-Changer in Treating Obesity
September 13, 2021
An estimated 650 million adults live with obesity today, which puts those individuals at increased risk for some of the leading causes of death worldwide,
Clinical Trial Shows In Vivo CRISPR-Cas9 Therapy Effective Against Rare Disease
August 22, 2021
Transthyretin amyloidosis (ATTR amyloidosis) is a rare but fatal disease marked by clumping and accumulation of mutated, misfolded transthyretin proteins in peripheral nerves and cardiac
Could Giraffes Advance Human Genetic Research?
August 18, 2021
Depending on your perspective, giraffes are either the world’s most graceful animal or a baffling, doe-eyed sloppy eater. (This could depend largely on whether you’re
New Eye Color Genetics Research Could Revolutionize Eye Disease Treatment
June 30, 2021
As a hereditary trait, eye color tends to be an introductory lesson to human genetics. Think back to high school biology class, which often covers
A Gene Therapy Startup Engages in Horseplay to Test New Osteoarthritis Therapy
June 21, 2021
Osteoarthritis is a debilitating and painful wearing down of joint cartilage tissues. Every year, more than three million people in the U.S. (and millions more
Understanding How Cells Tell RNA and DNA Apart Could Lead to New Antivirals
May 17, 2021
RNA viruses are known to cause a large number of diseases in humans, including COVID-19, measles, influenza, hepatitis, yellow fever and Zika. Most new and
Five Criteria to Use When Selecting a CRO for a Gene Therapy Study
April 26, 2021
Contract research organizations (CROs) have been an integral part of drug development since the 1920s, first as providers of preclinical testing services, then as organizations
How a Rare Breed of Rabbit Is Advancing Genetics
April 7, 2021
Although you might think of the ability to hop as one of rabbits’ defining characteristics, some rabbits don’t hop at all. The sauteur d’Alfort is a rare breed
Determining “Responsible Clinical Use” in Heritable Human Genome Editing
March 22, 2021
A common refrain in science fiction movies is the cautionary statement, “Just because we can doesn’t mean we should.” As new technologies such as CRISPR/Cas9
Robust Cell and Gene Therapy Pipeline Targets a Range of Diseases
March 1, 2021
Cell and gene therapies (CGTs) are quickly making their way from theory to clinical practice, primarily because they target specific disease drivers rather than the
The Genetics of Calico Cats
December 16, 2020
Whether you adore cats or you’re allergic to them, you might be surprised to learn that you can better understand genetics by studying calico cats.
Could Gene Therapy Hold the Answer to Danon Disease?
December 14, 2020
Danon Disease is a rare, life-threatening condition in which the body’s protein removal and recycling processes no longer work properly. The result is dysfunction of
Gene Therapy and Inherited Retinal Diseases
November 9, 2020
Inherited retinal diseases (IRDs) can cause vision loss that ranges from mild to severe, and can even cause blindness. These diseases affect people of all
Squid Genes: Self-Edits in the Wild and CRISPR Edits in the Lab
August 10, 2020
Squid have long been a key organism for deepening the understanding of how nerves transmit signals. They have been passed over for gene-editing studies, however,
CAR-T and CRISPR Cancer Trial Shows Promise
March 2, 2020
There is new hope for future innovation in the fast-moving field of cancer immunotherapy. Earlier this month, researchers from the University of Pennsylvania and Stanford
Gene Therapy Innovation Strongly Encouraged by FDA with New Guidances
February 10, 2020
On January 28, 2020, the United States Food and Drug Administration (FDA) announced the release of six final guidances on gene therapy manufacturing and the clinical
Skin Biopsy: A Complex Model Exploring Gene Expression
May 9, 2019
The heterogeneous presentation of clinical cases and the complex requirements by health authorities and care management contribute to making the development of innovative treatment options
Introduction Researchers are developing novel, safer treatments for cancer, but bringing new oncology therapies to market is challenging. This white paper will examine the…
Introduction As global obesity rates continue to rise, the search for effective treatments is more critical than ever. Obesity is associated with an increased…
Introduction Changes in how clinical trials are managed in the European Union (EU), mandated by the European Union Clinical Trial Regulation 536/2014 (EU CTR),…
NEWARK, Delaware, November 13, 2024/BUSINESS WIRE/ — QPS Holdings, LLC announced today that their Springfield campus, QPS Missouri, has launched a new Cell Therapy…
NEWARK, Delaware, June 26, 2024/BUSINESS WIRE/ — QPS Holdings, LLC (QPS), a leading global contract research organization (CRO), is pleased to announce new laboratory…
NEWARK, Delaware, June 10, 2024/BUSINESS WIRE/ — QPS Holdings, LLC (QPS), a leading global contract research organization (CRO), is pleased to announce new clinical…
